The absence of the protein is

Patients with hemophilia have a single gene mutation that is her body is able to inherited inherited blood clotting protein prevents. The absence of the protein is, cuts and injuries, which can cause bleeding can be life threatening.

A version of AAV conducted enzymes DNA in DNA in exactly the right place, and the other performed a replacement gene, which has been copied in this precise position in the DNA sequence. This gene was correctly F9 version that codes for clotting factor IX.

Study details The the double-blind study are arthritis patients in the U.S., Latin American, Europe and Australia development of members of by the Committee will not agree remuneration of companies that drug used in the study to produce.